Clinical trials in rare diseases are complex and present unique challenges. However, patients in these trials are very vocal, with caretakers, family members, and advocates eager to share their experiences. By using actionable strategies to find, listen to, and learn from patients themselves, researchers can include their perspective in study design.
Exploring the Puzzling World of Rare Diseases
Rare Diseases Advisory Committee
Rare Diseases Advisory Committee—PRA is proud to join forces with a group of highly skilled and experienced patient advocates — collectively working…
RARE DISEASES NEWSLETTER Volume 9, April 2018
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.