Rare Disease

Guiding Principles for Interactions with Rare Disease Patient Advocacy Organizations

PRA acknowledges and thanks the members of the Rare Disease Advisory Committee (RDAC) who provided their valuable contributions to the development of…

A Critical Success Factor in Rare Disease Clinical Research: Patient Advocacy Collaboration

In most public sectors, understanding the end user’s perspective and building out a product strategy around it is nothing short of dogma. However, in…

PRA Hosts Rare Disease Day Event

World Rare Disease Day (WRDD) is an important time to raise awareness for the 7,000+ known rare diseases and the millions of people whose daily lives…

RARE DISEASES NEWSLETTER Volume 15, December 2019

Research Expertise

Rare Diseases Advisory Committee

Rare Diseases Advisory Committee—PRA is proud to join forces with a group of highly skilled and experienced patient advocates — collectively working…

Rare Diseases Advisory Committee Members

Our Centers

Certain challenges within the drug development landscape merit a dedicatedtask force of experts and capabilities. That’s why we built our collection…

The Fight Against Rare Diseases

Collectively, rare diseases represent a large medical challenge. While most have no cure, the appropriate treatment can greatly improve quality of…

Strategies and Collaborations to Accelerate Rare Disease Clinical Development

Understanding the disease landscape and the competitive clinical trial environment when positioning a new clinical trial within the rare disease…