Clinical trials in rare diseases present unique challenges unseen in trials for more common conditions. Cross-border enrollment can be key to enrolling and retaining the required number of participants in a rare disease clinical trial. However this creates complex patient logistics and a regulatory maze that must be appropriately navigated. Understanding these considerations is critical to timely and successful study completion.
Rare Diseases Advisory Committee Members
The Patient Voice: Engaging Rare Disease Patients Improves Clinical Trial Enrollment & Retention
Clinical trials in rare diseases are complex and present unique challenges. However, patients in these trials are very vocal, with caretakers, family…
RARE DISEASES NEWSLETTER Volume 7, October 2017
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.