A Top 10 pharmaceutical client required a mobile technology solution to collect safety and effectiveness data on a groundbreaking treatment for an ultra-rare disease in a global gene therapy prospective registry. With a single principal investigator to oversee enrolled patients in several countries on 2 continents, Clinical6 provided a multilingual technology platform to engage patients, parents, caregivers, and local healthcare providers.
The Importance of Patient Education for Rare Disease Trials
Exploring the Puzzling World of Rare Diseases
Center for Rare Diseases continues to engage with rare disease patient communities during COVID-19 crisis
PRA Health Sciences’ Center for Rare Diseases is committed to engaging rare disease patient communities, and providing transparency, throughout the…