Innovative Technology Solution for a 15 Year Rare Disease Gene Therapy Registry

A Top 10 pharmaceutical client required a mobile technology solution to collect safety and effectiveness data on a groundbreaking treatment for an ultra-rare disease in a global gene therapy prospective registry. With a single principal investigator to oversee enrolled patients in several countries on 2 continents, Clinical6 provided a multilingual technology platform to engage patients, parents, caregivers, and local healthcare providers.