A Top 10 pharmaceutical client required a mobile technology solution to collect safety and effectiveness data on a groundbreaking treatment for an ultra-rare disease in a global gene therapy prospective registry. With a single principal investigator to oversee enrolled patients in several countries on 2 continents, Clinical6 provided a multilingual technology platform to engage patients, parents, caregivers, and local healthcare providers.
RARE DISEASES NEWSLETTER Volume 8, January 2018
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.
Improving Treatment for Rare Cancers
In recognition of World Cancer Day on February 4th, we explore questions around the latest rare cancer research, treatments, and how to improve…
RARE DISEASES NEWSLETTER Volume 13, May 2019
Welcome to the thirteenth edition of the rare diseases newsletter. This quarterly publication strives to keep you up to date on PRA's Center for Rare…