Champions of patient centricity express a need for evidence of the value of involving patients and patient-centric clinical development practices to help them drive adoption and organizational change.
This dossier outlines emerging evidence of benefits/ROI of patient involvement in the trial development process from recent literature and provides illustrative case studies from PRA’s Center for Rare Diseases.
Gene Therapy Research and Rare Diseases
Shortening the Path to Rare Disease Diagnosis with a Patient-Centric Approach
Many rare disease patients struggle for years before they know what their symptoms indicate, and even longer to find a meaningful treatment. Learn…
RARE DISEASES NEWSLETTER Volume 6, May 2017
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.