A phase II single-blind, randomized, placebo-controlled trial to study the efficacy and safety of Study Drug administered as adjunctive treatment to patients with acquired thrombotic thrombocytopenic purpura.
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Newsletter
RARE DISEASES NEWSLETTER Volume 6, May 2017
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.
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Fact Sheet
Rare Disease Fact Sheet
Clinical development involving rare diseases poses a unique set of medical, scientific, and operational challenges. PRA understands these challenges…
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Infographic
The Fight Against Rare Diseases
Collectively, rare diseases represent a large medical challenge. While most have no cure, the appropriate treatment can greatly improve quality of…
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