This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.
Gene Therapy Research and Rare Diseases
The Patient Voice: Engaging Rare Disease Patients Improves Clinical Trial Enrollment & Retention
Clinical trials in rare diseases are complex and present unique challenges. However, patients in these trials are very vocal, with caretakers, family…
The Center for Rare Diseases
We never forget that rare diseases alter entire lives—and we’re committed to changing that. Every day can be delayed, postponed, or canceled when…