This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.
Decoding FDA Gene Therapy Guidances Part Two: Rare Disease
In Part Two of Decoding FDA Gene Therapy Guidances, we discuss three separate guidances that provide further insight into how sponsors can safely and…
Rare Diseases and the Promise of Gene Therapy: What You Need to Know
Rare Diseases Advisory Committee
Rare Diseases Advisory Committee—PRA is proud to join forces with a group of highly skilled and experienced patient advocates — collectively working…