Understanding the disease landscape and the competitive clinical trial environment when positioning a new clinical trial within the rare disease space.
RARE DISEASES NEWSLETTER Volume 10, July 2018
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.
Partnering with Patients to Develop Meaningful Endpoints – Practical Considerations
Selection of appropriate endpoints for rare disease clinical studies can be challenging but is critical to assessing the efficacy of new medicines.…
What to ask for when you’re interested in a clinical trial: A guide for rare disease patients and caregivers
Considering a clinical trial? This handy guide will help you ask about the support you’ll receive to make your participation easier and make informed…