Understanding the disease landscape and the competitive clinical trial environment when positioning a new clinical trial within the rare disease space.
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Newsletter
RARE DISEASES NEWSLETTER Volume 10, July 2018
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.
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White Paper
Partnering with Patients to Develop Meaningful Endpoints – Practical Considerations
Selection of appropriate endpoints for rare disease clinical studies can be challenging but is critical to assessing the efficacy of new medicines.…
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Resource
What to ask for when you’re interested in a clinical trial: A guide for rare disease patients and caregivers
Considering a clinical trial? This handy guide will help you ask about the support you’ll receive to make your participation easier and make informed…
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