Rare disease trials differ from those in most other therapeutic areas because the indications are more complex and involve smaller patient populations. It is essential to understand the current disease landscape, the prior research, and the competitive clinical trial environment when posi¬tioning a new clinical trial within the rare disease space. This white paper discusses strategies for accelerating rare disease clinical development by lever¬aging data in a more evidence-based approach to guide the design of a trial; to understand treat¬ment trends; and to identify the best investigators, sites, and patients.
Clinical Trial Manager
A PRA Clinical Trial Manager leads and manages the execution of one or more clinical studies from study startup through database release. As a core…
Rare Diseases Newsletter Volume 16, April 2020
Clinical Research Associate
PRA Clinical Research Associates (CRAs) choose one of two career paths. They may work onsite with one of our top pharmaceutical clients. Or they may…