Collectively, rare diseases represent a large medical challenge. While most have no cure, the appropriate treatment can greatly improve quality of life and extend life expectancy. Impressive progress has been made, so we must not give up the fight. A disease might be rare, but hope should not be.
RARE DISEASES NEWSLETTER Volume 5, January 2017
This quarterly publication will keep you up to date on PRA’s Rare Disease Team focus, achievements, and new initiatives.