PRA is proud to join forces with a group of highly skilled and experienced patient advocates — collectively working towards improving the way patients with rare diseases are integrated into the clinical development lifecycle.
About the Committee
The Rare Diseases Advisory Committee (RDAC) is an independent and autonomous volunteer group that advises and works with PRA’s Center for Rare Diseases. Together they work to better understand the ways in which clinical trials can be revolutionized to be more effective and accessible for these patients and their unique challenges.
The inaugural committee members are a group comprised of experienced and talented individuals, all with a deep connection to the rare diseases community.
About the Collaboration
Working alongside the RDAC is the international team of experts at PRA’s Center for Rare Diseases. This team has dedicated itself to groundbreaking research and the development of life-changing therapies — specifically for patients with rare diseases. Since 2012, the Center has served more than 50,000 patients in over 300 clinical studies, leading to 18 approved drugs that fight rare diseases.
Creating Solutions to Ensure Endpoint Protection in Challenging Rare Disease Trial
The collection of high-quality endpoint data was paramount to the success of this Phase II program. Because this was the first clinical trial ever…
The Fight Against Rare Diseases
Collectively, rare diseases represent a large medical challenge. While most have no cure, the appropriate treatment can greatly improve quality of…
The Future of Clinical Trials: Connected and Virtual Approaches for Rare Diseases
Scott Schliebner, Senior Vice President, Center for Rare Diseases at PRA Health Sciences talks about how amore patient-centred approach is needed to…